Dedicated to making life better for people with rare and serious diseases

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Our proprietary personalized gene therapy platform

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personalized biologics approach

Our focus on the patient drives everything we do and as a result, our path forward is clear: to develop game-changing gene therapies for localized treatment of rare and serious diseases.

— John Maslowski, Chief Executive Officer

Our robust development pipeline of personalized therapies for localized treatment

Applying the unique characteristics of autologous fibroblasts to gene therapies

Photo left: Courtesy of debra–The Dystrophic Epidermolysis Bullosa Research Association of America. Used with permission.
Photo right: Courtesy of debra–The Dystrophic Epidermolysis Bullosa Research Association of America. Used with permission.

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